The Give Kids a Chance Act is a bipartisan bill that includes the reauthorization of the Rare Pediatric Disease Priority Review Voucher (PRV). This program plays a vital role in offering hope to the millions of children in the U.S. affected by rare diseases – 30% of whom will not reach their fifth birthday. The PRV program has driven innovation, benefiting over 200,000 patients and addressing significant unmet medical needs across 47 rare pediatric conditions—all with minimal to no cost to taxpayers.
When the Priority Voucher Program lapsed last year, we promised to keep fighting to protect the future of the rare disease community. Today, we follow up on that promise. We strongly support the Give Kids a Chance Act reintroduced in Congress yesterday, to restore and extend the Rare Pediatric Disease Priority Voucher Review Program. Backed by bipartisan leaders, this program has already benefited more than 200,000 patients among 47 rare disease indications. It’s a cost-effective and innovative avenue to address the more than 95% of rare diseases out there with no approved therapy. We are deeply appreciative to the bill’s sponsors for working to protect this invaluable program: - Congressman Michael McCaul (TX-10) - Congressman Gus Bilirakis (R-FL) - Congresswoman Debbie Dingell (D-MI) - Congresswoman Kim Schrier (D-WA) - Congresswoman Diana Harshbarger (R-TN.) - Congresswoman Kathy Castor (D-FL) - Congressman Mike Kelly (R-PA) - Congresswoman Doris Matsui (D-CA) - Congressman Dan Crenshaw (R-TX) - Congresswoman Lori Trahan (D-MA) - Congressman Randy Weber (R-TX) Now, let’s get the job done.
