药明康德

Dr. Annette Bakker, CEO of the Children's Tumor Foundation (CTF), has spent the last decade passionately devoted to finding impactful therapies to treat all forms of neurofibromatosis (NF), genetically-driven rare disease-causing tumors to grow on nerves. Under her leadership, CTF has built global, patient-centric research networks that not only benefit NF patients but has broadened awareness of NF. Notably, the Foundation also engaged in 2 novel drug approvals for NF1 and drugs in clinical testing for NF2-SWN, and has been advocating for a blueprint in accelerating rare disease drug development. In our fourth interview of this series, Dr. Bakker shares her insights on the role of patient organizations, key factors for successful partnerships, and her call to action in rare disease drug development: https://lnkd.in/e-xMS8Qa

For many, awareness of ALS (amyotrophic lateral sclerosis) grew through the Ice Bucket Challenge of 2014, a viral social media movement that raised unprecedented funds and attention for research. ALS remains one of the most devastating neurodegenerative diseases, gradually stripping individuals of their ability to move, speak, and breathe while leaving their cognitive functions intact. A decade later, in our third installment of the Rare Disease Interview Series, we sit down with Calaneet Balas, President and CEO of The ALS Association, to reflect on the progress made since that pivotal moment. She shares insights on the evolving landscape of ALS research, the lasting impact of the Ice Bucket Challenge, and the urgent need for innovation and collaboration to drive the next breakthroughs in treatment: https://lnkd.in/eqZxKQyQ

Children with rare diseases are often described as the orphans of medicine—overshadowed, misdiagnosed, and forced to endure a relentless odyssey from doctor to doctor. Many of these conditions remain incurable, leaving affected children and their families with little hope for a better future. However, through increased research efforts and robust international cooperation, this grim fate can be transformed.   In this second interview of our Rare Disease Series, we speak with Prof. Christoph Klein, a leading figure in pediatric medicine and visionary founder of the Care-for-Rare Foundation. His insights reveal how cross-disciplinary collaboration is reshaping rare disease treatment and bringing us closer to a world where no child is left behind. https://lnkd.in/e3arvxVQ

On Rare Disease Day, we come together to raise global awareness and inspire innovation. To mark this occasion, we are delighted to spotlight insights from leading experts in the field.   Our series begins with Dr. Stanley Crooke. As the founder of Ionis Pharmaceuticals 35 years ago, Dr. Crooke and his team pioneered antisense technology, transforming drug development in neurology, cardiology, rare diseases, and other specialty areas. Today, with n-Lorem Foundation, Dr. Crooke has turned his focus to the "nano-rare"—patients often overlooked by traditional healthcare models. His mission at n‑Lorem is simple yet profound: to deliver personalized RNA-targeted therapies to patients with nano‑rare diseases, ensuring that even the rarest conditions are met with innovative, life-changing treatments: https://lnkd.in/gCUNSt2e

WuXi AppTec is expanding our European presence to provide partners with faster, more efficient, and higher-quality solutions for scientific breakthroughs in the pharmaceutical, biotech and life sciences industries. Through continuous investment in our capacity and capabilities, we are strengthening our #CRDMO model to better support innovation and deliver life-changing therapies to patients worldwide. Discover here how our Swiss and German facilities are enabling breakthroughs in Europe and beyond. #LifeSciences #BiotechEurope #Switzerland #Germany

On International Day of Women and Girls in Science, we celebrate the incredible women scientists working across global healthcare for their unwavering commitment to progress toward a healthier world.    Women represent more than 50% of WuXi AppTec’s global workforce. Their expertise and dedication contribute to meaningful change for patients every day. Together, we are building a future where every drug can be made, and every disease can be treated.

Last week, the 2025 WuXi Global Forum brought together thousands of leaders, innovators, and visionaries from around the world to share ideas and spark meaningful collaborations. Today, we’re excited to share the digital premiere of the event, including highlights from the opening plenary, with over 120 executive roundtables led by C-Suite leaders. Join us in celebrating the progress we’ve made and the shared journey that unites us all in transforming patients’ lives.   Every Innovation Story Matters: https://lnkd.in/dcYz_nEc

Thank you to our friends and colleagues who joined us yesterday for our 13th annual WuXi Global Forum at #JPM2025. Your presence and engagement reflect the true essence of our industry: a shared journey of knowledge, collaboration, and advancement for patients. We are especially grateful to our distinguished panelists and executive roundtable hosts for sharing their insights and expertise. Your contributions continue to push the boundaries of innovation and collaboration within the global healthcare community. It was inspiring to witness the collective wisdom, forward-thinking ideas, and partnerships that emerged during the Forum’s more than 120 executive roundtables. Together, we are advancing new solutions that will shape the future of healthcare.

We're pleased to announce that WuXi AppTec has joined the Pharmaceutical Supply Chain Initiative (#PSCI) as a Supplier Partner! This underscores the company’s enduring commitment to responsible business practices and supply chain resilience.   By adhering to PSCI standards and enhancing our value chain management, we remain dedicated to supporting our customers in delivering innovative new therapies to #patients, working together towards a healthier and more sustainable future.   Read more: https://lnkd.in/ejzC-esU

Entering its 13th year, the WuXi Global Forum will be held next week in #SanFrancisco during the 2025 J.P. Morgan Healthcare Conference. This year's event will kick off with "State of Innovation" followed by more than 100 Executive Roundtables. At the Forum, Every Innovation Story Matters. https://lnkd.in/eMjM_BtF