Brain and Nervous System News, Features & Updates

September 21, 2026 — The FDA has approved Fayuvi (rebisufligene etisparvovec) for the treatment of neurologic manifestations of mucopolysaccharidosis type IIIA (MPS IIIA), also called Sanfilippo syndrome type A, in pediatric patients with preserved neurodevelopmental function.

September 14, 2026 — The FDA has approved Isembyld (apitegromab) for spinal muscular atrophy (SMA) in adults and children 2 years of age and older who are currently receiving an SMN2-targeted treatment.

September 4, 2026 — The FDA has approved Zanvastro (zilganersen) for the treatment of Alexander disease in children and adults.

A myasthenia gravis specialist shares strategies for getting the most out of your relationship with your MG care team.

A myasthenia gravis expert explains current and emerging treatments for the disease.

A neurologist answers the most common questions about living with myasthenia gravis in this Reddit AMA.

A neurology and neuromuscular medicine specialist shares details on newer treatment options for myasthenia gravis that expand care for people with the condition.

A neurologist shares expert tips on how to manage the fatigue of myasthenia gravis and use your energy wisely.

December 12, 2025 — Uplizna (inebilizumab-cdon) is a prescription medicine recently approved by the FDA to treat adults with generalized myasthenia gravis (gMG) who test positive for certain antibodies.

If you’ve been diagnosed with Lambert Eaton myasthenic syndrome, this article will explain to you the latest diagnostic tests and treatments for this autoimmune syndrome.

Lambert-Eaton syndrome is a rare disease, but many people successfully live with the condition. Here, one patient advocate shares his story.

A leading expert on Lambert-Eaton syndrome offers insights on causes, symptoms, and what’s new with treatment for this rare condition.

November 25, 2025 — The FDA has approved Itvisma (onasemnogene abeparvovec-brve) as a gene therapy to treat spinal muscular atrophy (SMA) in adults, teens, and children 2 or older who have a mutation in the survival motor neuron 1 (SMN1) gene.

November 21, 2025 — The FDA has approved the oral medication selumetinib (Koselugo) for adults with neurofibromatosis type 1 (NF1) who have tumors called plexiform neurofibromas (PN) that are symptomatic and cannot be surgically removed.

Learn tips and strategies from an expert for what to expect when you have myasthenia gravis and how to make the most of your treatment.

Learn what to do when your treatment for myasthenia gravis is not working.

Find out the latest treatments for myasthenia gravis.

Misha Grayson Coleman describes what it’s like living with myasthenia gravis, and what she wishes she had known about it.

Myasthenia gravis is a challenging disease. But with new FDA-approved drugs and teamwork, “hitting the wall” might be a chance to find new answers.

Neurofibromatosis is a rare disease that can be crippling. New treatments can help, and more are on the way. Learn about recent advances for NF.

This rare disease causes a list of symptoms, including tumors, skin changes, and hearing loss. Our expert answers your pressing questions about how it’s treated, what you can expect, and more.

Diane Owens does not watch or wait when it comes to being a parent of a child with NF. She’s working, running, and keeping the faith.

Learn about a new drug for myasthenia gravis. A top expert explains nipocalimab (Imaavy) and its benefits, how it works, and its impact on MG treatment.

The FDA has approved nipocalimab, a myasthenia gravis treatment designed to help control the disease better over time. Learn how it works and who it might help.

May 2, 2025 — The FDA approves Imaavy, a groundbreaking treatment for generalized myasthenia gravis (gMG), offering symptom relief and reduced autoantibody levels in adults and children over 12.

Creatine has long been used as an athletic performance enhancer. Does it also help the brain? Find out what researchers are learning.

March 11, 2025 — The FDA approved Soliris for children aged 6 and older with generalized myasthenia gravis (gMG), offering new hope for managing this autoimmune neuromuscular disorder.

Richard Nowak, MD, director of the Myasthenia Gravis Clinic at the Yale School of Medicine, discusses advances made in MG treatment and care over the last decade.

Ashley Brooks talks about the unique challenges of navigating MG as a Black woman.

February 24, 2025 — The FDA has approved a new pill for adults with cerebrotendinous xanthomatosis (CTX), a rare genetic disease that makes it hard for the body to handle cholesterol properly.

February 4, 2025 — Microplastics have been found in the brain, showing they can cross the blood-brain barrier, and the amounts of the tiny plastic bits inside our bodies appear to be increasing at a rate that reflects the increasing amount of global plastic waste.

January 28, 2025 — Voice disorders are on the rise. We asked experts how to keep speaking loud and clear.

An individual living with myasthenia gravis explains how they came to accept and love their life after diagnosis.

A doctor discusses new treatments for myasthenia gravis in the research pipeline and how they may improve patients’ lives.

An MG patient and advocate talks about her advocacy work to help improve life for other people with MG.

October 29, 2024 — New evidence suggests that rapidly shaking your head after a big hit could indicate a serious brain injury. But why do people do that, anyway?

July 31, 2024 — Pivotal phase III trial data has been released for drug, a special type of protein that stops a harmful reaction in the body that could make Guillain-Barre symptoms worse.

April 5, 2024 — Investigators have created the first images that accurately depict facial distortions experienced by people with PMO, a rare visual disorder that is often mistaken for mental illness.

March 29, 2024 — The CDC is warning health care providers in the United States to be on the watch for a rare bacterial illness that can lead to meningitis and possibly death.

A doctor who treats myasthenia gravis patients details how treatment has evolved and how new treatment options have affected management of the condition.

Navigating a myasthenia gravis diagnosis as a young adult and in a rigid health care system, a young woman advocates for herself and her health.

Hereditary transthyretin amyloidosis (hATTR) with polyneuropathy is rare, but with diagnosis through genetic testing, you can find answers and treatment.

A look at how hATTR advances, and working with your doctor to get palliative and end-of-life care.

January 10, 2024 — A new study from Harvard University’s Massachusetts Eye and Ear offers groundbreaking insight into the role the brain plays in tinnitus – and its surprising significance.

December 27, 2023 — People who lived alone with pets had slower rates of cognitive decline based on those test results when compared to people who lived entirely alone.

A doctor who regularly treats myasthenia gravis patients details what he has learned from them and how he applies those lessons to his own life.

A patient living with myasthenia gravis talks about the most helpful – and hurtful – advice she has received since her diagnosis.

November 6, 2023 — Older people enrolled in tai chi classes showed improved performance on memory tests, especially if they took a more challenging form of the exercise, says a study published in the Annals of Internal Medicine.

November 2, 2023 — We know being creative is good for your brain and mental health -- and you can get better at it. Here are eight ways.